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Preserved outer retina in AIPL1 Leber's congenital amaurosis: Implications for gene therapy

  • Jonathan Aboshiha
  • , Adam M. Dubis
  • , Jacqueline Van Der Spuy
  • , Koji M. Nishiguchi
  • , Edward W. Cheeseman
  • , Carmen Ayuso
  • , Miriam Ehrenberg
  • , Francesca Simonelli
  • , James W. Bainbridge
  • , Michel Michaelides*
  • *Corresponding author for this work
  • University College London
  • Moorfields Eye Hospital NHS Foundation Trust
  • Medical University of South Carolina
  • IIS-Fundacion Jiménez Díaz
  • Schneider Childrens Medical Center Israel
  • University of Campania Luigi Vanvitelli

Research output: Contribution to journalArticlepeer-review

31 Scopus citations
Original languageEnglish
Pages (from-to)862-864
Number of pages3
JournalOphthalmology
Volume122
Issue number4
DOIs
StatePublished - 1 Apr 2015
Externally publishedYes

Funding

FundersFunder number
National Institutes of HealthR01EY017607

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