Preserved outer retina in AIPL1 Leber's congenital amaurosis: Implications for gene therapy

Jonathan Aboshiha, Adam M. Dubis, Jacqueline Van Der Spuy, Koji M. Nishiguchi, Edward W. Cheeseman, Carmen Ayuso, Miriam Ehrenberg, Francesca Simonelli, James W. Bainbridge, Michel Michaelides*

*Corresponding author for this work

Research output: Contribution to journalArticlepeer-review

28 Scopus citations
Original languageEnglish
Pages (from-to)862-864
Number of pages3
JournalOphthalmology
Volume122
Issue number4
DOIs
StatePublished - 1 Apr 2015
Externally publishedYes

Funding

FundersFunder number
National Institutes of HealthR01EY017607

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