Lentiviral gene therapy corrects platelet phenotype and function in patients with Wiskott-Aldrich syndrome

  • Lucia Sereni
  • , Maria Carmina Castiello
  • , Dario Di Silvestre
  • , Patrizia Della Valle
  • , Chiara Brombin
  • , Francesca Ferrua
  • , Maria Pia Cicalese
  • , Loris Pozzi
  • , Maddalena Migliavacca
  • , Maria Ester Bernardo
  • , Claudio Pignata
  • , Roula Farah
  • , Lucia Dora Notarangelo
  • , Nufar Marcus
  • , Lorella Cattaneo
  • , Marco Spinelli
  • , Stefania Giannelli
  • , Marita Bosticardo
  • , Koen van Rossem
  • , Armando D'Angelo
  • Alessandro Aiuti, Pierluigi Mauri, Anna Villa*
*Corresponding author for this work

Research output: Contribution to journalArticlepeer-review

51 Scopus citations

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Medicine and Dentistry

Biochemistry, Genetics and Molecular Biology

Immunology and Microbiology