Early access experience with VPRIV®: Recommendations for 'core data' collection

Derralynn A. Hughes; Moeen Al-Sayed; Nadia Belmatoug; Olaf Bodamer; Tobias Böttcher; Maria Cappellini; Ian J. Cohen; Terence Eagleton; Deborah Elstein; Pilar Giraldo; Simon Jones; Chaim Kaplinsky; Allan Lund; Maciej Machaczka; Eugen Mengel; Gregory M. Pastores; Hanna Rosenbaum; Malvin Sjo; Nikolaus Tiling; Panagiotis Tsaftaridis; Ari Zimran; Neal Weinreb

doi:10.1016/j.bcmd.2010.10.015

Early access experience with VPRIV®: Recommendations for 'core data' collection

Derralynn A. Hughes^*, Moeen Al-Sayed, Nadia Belmatoug, Olaf Bodamer, Tobias Böttcher, Maria Cappellini, Ian J. Cohen, Terence Eagleton, Deborah Elstein, Pilar Giraldo, Simon Jones, Chaim Kaplinsky, Allan Lund, Maciej Machaczka, Eugen Mengel, Gregory M. Pastores, Hanna Rosenbaum, Malvin Sjo, Nikolaus Tiling, Panagiotis TsaftaridisAri Zimran, Neal Weinreb

^*Corresponding author for this work

Clinical Departments

Research output: Contribution to journal › Letter › peer-review

4 Scopus citations

Original language	English
Pages (from-to)	140-142
Number of pages	3
Journal	Blood Cells, Molecules, and Diseases
Volume	47
Issue number	2
DOIs	https://doi.org/10.1016/j.bcmd.2010.10.015
State	Published - 15 Aug 2011

Funding

Funders	Funder number
Gaucher Registry), Shire
Protalix
Shire HGT
Pfizer
Genzyme
Actelion Pharmaceuticals
Shire

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10.1016/j.bcmd.2010.10.015

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Hughes, D. A., Al-Sayed, M., Belmatoug, N., Bodamer, O., Böttcher, T., Cappellini, M., Cohen, I. J., Eagleton, T., Elstein, D., Giraldo, P., Jones, S., Kaplinsky, C., Lund, A., Machaczka, M., Mengel, E., Pastores, G. M., Rosenbaum, H., Sjo, M., Tiling, N., ... Weinreb, N. (2011). Early access experience with VPRIV®: Recommendations for 'core data' collection. Blood Cells, Molecules, and Diseases, 47(2), 140-142. https://doi.org/10.1016/j.bcmd.2010.10.015

@article{706334b3ffaf4c03971fe701cc491cbd,

title = "Early access experience with VPRIV{\textregistered}: Recommendations for 'core data' collection",

author = "Hughes, {Derralynn A.} and Moeen Al-Sayed and Nadia Belmatoug and Olaf Bodamer and Tobias B{\"o}ttcher and Maria Cappellini and Cohen, {Ian J.} and Terence Eagleton and Deborah Elstein and Pilar Giraldo and Simon Jones and Chaim Kaplinsky and Allan Lund and Maciej Machaczka and Eugen Mengel and Pastores, {Gregory M.} and Hanna Rosenbaum and Malvin Sjo and Nikolaus Tiling and Panagiotis Tsaftaridis and Ari Zimran and Neal Weinreb",

note = "Funding Information: Neil Weinreb has research grants from Genzyme and Shire, is on the speakers bureau for Genzyme Shire and is on Scientific Advisory Boards and has received honoraria from Genzyme (the Gaucher Registry), Shire (the therapeutic goals taskforce), and Pfizer/Protalix. Funding Information: Maciej Machaczka has received travel reimbursement, honoraria and research support from Genzyme Corporation, Actelion Pharmaceuticals and Shire HGT. Funding Information: Olaf Bodamer has received research funding from Shire and honoraria for lectures. ",

year = "2011",

month = aug,

day = "15",

doi = "10.1016/j.bcmd.2010.10.015",

language = "אנגלית",

volume = "47",

pages = "140--142",

journal = "Blood Cells, Molecules, and Diseases",

issn = "1079-9796",

publisher = "Academic Press Inc.",

number = "2",

}

Hughes, DA, Al-Sayed, M, Belmatoug, N, Bodamer, O, Böttcher, T, Cappellini, M, Cohen, IJ, Eagleton, T, Elstein, D, Giraldo, P, Jones, S, Kaplinsky, C, Lund, A, Machaczka, M, Mengel, E, Pastores, GM, Rosenbaum, H, Sjo, M, Tiling, N, Tsaftaridis, P, Zimran, A & Weinreb, N 2011, 'Early access experience with VPRIV®: Recommendations for 'core data' collection', Blood Cells, Molecules, and Diseases, vol. 47, no. 2, pp. 140-142. https://doi.org/10.1016/j.bcmd.2010.10.015

TY - JOUR

T1 - Early access experience with VPRIV®

T2 - Recommendations for 'core data' collection

AU - Hughes, Derralynn A.

AU - Al-Sayed, Moeen

AU - Belmatoug, Nadia

AU - Bodamer, Olaf

AU - Böttcher, Tobias

AU - Cappellini, Maria

AU - Cohen, Ian J.

AU - Eagleton, Terence

AU - Elstein, Deborah

AU - Giraldo, Pilar

AU - Jones, Simon

AU - Kaplinsky, Chaim

AU - Lund, Allan

AU - Machaczka, Maciej

AU - Mengel, Eugen

AU - Pastores, Gregory M.

AU - Rosenbaum, Hanna

AU - Sjo, Malvin

AU - Tiling, Nikolaus

AU - Tsaftaridis, Panagiotis

AU - Zimran, Ari

AU - Weinreb, Neal

N1 - Funding Information: Neil Weinreb has research grants from Genzyme and Shire, is on the speakers bureau for Genzyme Shire and is on Scientific Advisory Boards and has received honoraria from Genzyme (the Gaucher Registry), Shire (the therapeutic goals taskforce), and Pfizer/Protalix. Funding Information: Maciej Machaczka has received travel reimbursement, honoraria and research support from Genzyme Corporation, Actelion Pharmaceuticals and Shire HGT. Funding Information: Olaf Bodamer has received research funding from Shire and honoraria for lectures.

PY - 2011/8/15

Y1 - 2011/8/15

UR - http://www.scopus.com/inward/record.url?scp=79960837392&partnerID=8YFLogxK

U2 - 10.1016/j.bcmd.2010.10.015

DO - 10.1016/j.bcmd.2010.10.015

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C2 - 21146428

AN - SCOPUS:79960837392

SN - 1079-9796

VL - 47

SP - 140

EP - 142

JO - Blood Cells, Molecules, and Diseases

JF - Blood Cells, Molecules, and Diseases

IS - 2

ER -

Early access experience with VPRIV®: Recommendations for 'core data' collection

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