Coupling AAV-mediated promoterless gene targeting to SaCas9 nuclease to efficiently correct liver metabolic diseases

Alessia De Caneva, Fabiola Porro, Giulia Bortolussi, Riccardo Sola, Michela Lisjak, Adi Barzel, Mauro Giacca, Mark A. Kay, Kristian Vlahovicek, Lorena Zentilin, Andrés F. Muro*

*Corresponding author for this work

Research output: Contribution to journalArticlepeer-review

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Medicine & Life Sciences