Keyphrases
Clinical Efficacy
100%
Cystic Fibrosis Transmembrane Conductance Regulator
100%
Cystic Fibrosis
100%
I1234V
100%
Modulator Therapy
100%
Forced Expiratory Volume in 1 Second (FEV1)
80%
CFTR Modulators
60%
Body Mass Index
40%
Compound Heterozygous mutation
40%
Sweat Chloride
40%
Lung Clearance Index
40%
Amino Acids
20%
Missense mutation
20%
Study Support
20%
In Vitro Effect
20%
Misfolding
20%
Clinical Benefit
20%
Index Score
20%
Clinical Records
20%
Pseudomonas
20%
Cryptic Splice Site
20%
Airway Infection
20%
Pancreatic Insufficient
20%
Observational Descriptive Study
20%
F508del
20%
Chloride Measurement
20%
Minimal Function
20%
Intestinal Organoids
20%
Tezacaftor-ivacaftor
20%
Elexacaftor-tezacaftor-ivacaftor
20%
Human Bronchial Cells
20%
CFTR Modulator Therapy
20%
Biochemistry, Genetics and Molecular Biology
Cystic Fibrosis Transmembrane Conductance Regulator
100%
Cystic Fibrosis
100%
Body Mass
50%
Lung Clearance
50%
Ivacaftor
50%
Amino Acids
25%
Missense Mutation
25%
Pseudomonas
25%
Forced Expiratory Volume
25%
Immunology and Microbiology
Cystic Fibrosis Transmembrane Conductance Regulator
100%
Body Mass
66%
Lung Clearance
66%
Missense Mutation
33%
Pseudomonas
33%
Organoid
33%
Forced Expiratory Volume
33%
Amino Acid
33%
Airway
33%
Pharmacology, Toxicology and Pharmaceutical Science
Cystic Fibrosis Transmembrane Conductance Regulator
100%
Cystic Fibrosis
100%
Ivacaftor
50%
Tezacaftor
50%
Amino Acid
25%
Pseudomonas
25%
Respiratory Tract Infection
25%
Neuroscience
Cystic Fibrosis
100%
Cystic Fibrosis Transmembrane Conductance Regulator
100%
Body Mass Index
50%
Ivacaftor
50%
Amino Acid
25%
In Vitro
25%
Missense Mutation
25%